Titre : | Survival in patients diagnosed with SMA at less than 24 months of age in a population-based setting before, during and after introduction of nusinersen therapy. Experience from Sweden |
Revue : | European journal of paediatric neurology : EJPN : official journal of the European Paediatric Neurology Society, 40 |
Auteurs : | Berglund A ; Berko S ; Lampa E ; Sejersen T |
Type de document : | Article |
Editeur : | England, 09/2022 |
Pages : | p 57 |
Langues: | Anglais |
Mots-clés: | Mortality; Nusinersen; SMA; Spinal muscular atrophy; Survival; |
Pubmed / DOI : | Pubmed : 35973318 / DOI : 10.1016/j.ejpn.2022.07.005 |
N° Profil MNM : | 2022082 |
En ligne : | http://www.ncbi.nlm.nih.gov/pubmed/35973318 |