Title: | Nusinersen efficacy data for 24-month in type 2 and 3 spinal muscular atrophy |
Journal : | Annals of clinical and translational neurology, 9, 3 |
Authors: | Pane M ; Coratti G ; Pera MC ; Sansone VA ; Messina S ; D'Amico A ; Bruno C ; Salmin F ; Albamonte E ; De Sanctis R ; Sframeli M ; Di Bella V ; Morando S ; Palermo C ; Frongia AL ; Antonaci L ; Capasso A ; Catteruccia M ; Longo A ; Ricci M ; Cutrona C ; Pirola A ; Bravetti C ; Pedemonte M ; Brolatti N ; Bertini E ; Mercuri E |
Material Type: | Article |
Publisher: | United States, 03/2022 |
Size: | p 404 |
Languages: | English |
Keywords : | comparative studies ; medical monitoring ; motor skills ; nusinersen ; spinal muscular atrophy ; therapeutic efficiency |
Pubmed / DOI : | Pubmed : 35166467 / DOI : 10.1002/acn3.51514 |
N° Profil MNM : | 2022022 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/35166467 |