Titre : | Clinical efficacy of the enzyme replacement therapy in patients with late-onset Pompe disease: a systematic review and a meta-analysis |
Revue : | Journal of neurology |
Auteurs : | Sarah B ; Giovanna B ; Emanuela K ; Nadi N ; Josè V ; Alberto P |
Type de document : | Article |
Editeur : | Germany, 13/04/2021 |
Langues: | Anglais |
Mots-clés: | Enzyme replacement therapy;Gycogen storage disease type II;Late-onset Pompe disease;Meta-analyse;Pompe disease;Recombinant human alpha-glucosidase;Systematic review; |
Pubmed / DOI : | Pubmed : 33851281 / DOI : 10.1007/s00415-021-10526-5 |
N° Profil MNM : | 2021042 |
En ligne : | http://www.ncbi.nlm.nih.gov/pubmed/33851281 |