Title: | Parents' perspectives on nusinersen treatment for children with spinal muscular atrophy |
Journal : | Developmental medicine and child neurology |
Authors: | van Kruijsbergen M ; Schroder CD ; Ketelaar M ; van der Pol WL ; Cuppen I ; van der Geest A ; Asselman FL ; Fischer MJ ; Visser-Meily JMA ; Kars MC |
Material Type: | Article |
Publisher: | England, 06/02/2021 |
Languages: | English |
Pubmed / DOI : | Pubmed : 33550591 / DOI : 10.1111/dmcn.14825 |
N° Profil MNM : | 2021021 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/33550591 |