Title: | Reldesemtiv in Patients with Spinal Muscular Atrophy: a Phase 2 Hypothesis-Generating Study |
Journal : | Neurotherapeutics |
Authors: | Rudnicki SA ; Andrews JA ; Duong T ; Cockroft BM ; Malik FI ; Meng L ; Wei J ; Wolff AA ; Genge A ; Johnson NE ; Tesi-Rocha C ; Connolly AM ; Darras BT ; Felice K ; Shieh PB ; Mah JK ; Statland J ; Campbell C ; Habib AA ; Kuntz NL ; Oskoui M ; Day JW |
Material Type: | Article |
Publisher: | United States, 23/02/2021 |
General note: | Erratum in: Erratum. [Neurotherapeutics. 2021] |
Languages: | English |
Keywords: | Reldesemtiv;pharmacodynamics;pharmacokinetics;six-minute walk test;spinal muscular atrophy clinical trial; |
Pubmed / DOI : | Pubmed : 33624184 / DOI : 10.1007/s13311-020-01004-3 |
N° Profil MNM : | 2021022 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/33624184 |
See also : |