Titre : | The Identification of Novel Biomarkers Is Required to Improve Adult SMA Patient Stratification, Diagnosis and Treatment |
Revue : | Journal of personalized medicine, 10, 3 |
Auteurs : | Smeriglio P ; Langard P ; Querin G ; Biferi MG |
Type de document : | Article |
Editeur : | Switzerland, 2020 |
Langues: | Anglais |
Mots-clés: | -omics approaches;Nusinersen;adult patients;biomarkers;disease heterogeneity;disease modifiers;epigenetic changes;functional outcomes;spinal muscular atrophy; |
Pubmed / DOI : | Pubmed : 32751151 / DOI : 10.3390/jpm10030075 |
N° Profil MNM : | 2020081 |
En ligne : | http://www.ncbi.nlm.nih.gov/pubmed/32751151 |