Title: | Expanded access program with Nusinersen in SMA type I in Italy: Strengths and pitfalls of a successful experience |
Journal : | Neuromuscular disorders : NMD, 27, 12 |
Authors: | Messina S ; Pane M ; Sansone V ; Bruno C ; Catteruccia M ; Vita G ; Palermo C ; Albamonte E ; Pedemonte M ; Bertini E ; Binetti L ; Mercuri E |
Material Type: | Article |
Publisher: | England, 06/2017 |
Size: | p 1084 |
Languages: | English |
Pubmed / DOI : | Pubmed : 29132728 / DOI : 10.1016/j.nmd.2017.09.006 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/29132728 |