Title: | Applying genome-wide CRISPR-Cas9 screens for therapeutic discovery in facioscapulohumeral muscular dystrophy |
Journal : | Science translational medicine, 12, 536 |
Authors: | Lek A ; Zhang Y ; Woodman KG ; Huang S ; DeSimone AM ; Cohen J ; Ho V ; Conner J ; Mead L ; Kodani A ; Pakula A ; Sanjana N ; King OD ; Jones PL ; Wagner KR ; Lek M ; Kunkel LM |
Material Type: | Article |
Publisher: | United States, 03/2020 |
Languages: | English |
Keywords : | CRISPR/Cas9 ; facioscapulohumeral muscular dystrophy ; molecular screening ; therapeutical research |
Pubmed / DOI : | Pubmed : 32213627 / DOI : 10.1126/scitranslmed.aay0271 |
N° Profil MNM : | 2020032 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/32213627 |