Title: | Gene therapies for axonal neuropathies: Available strategies, successes to date, and what to target next |
Journal : | Brain research |
Authors: | Morelli KH ; Hatton CL ; Harper SQ ; Burgess RW |
Material Type: | Article |
Publisher: | Netherlands, 04/2020 |
Languages: | English |
Keywords : | Becker muscular dystrophy ; Charcot-Marie-Tooth disease ; Duchenne muscular dystrophy ; gene therapy ; neuromuscular disease ; peripheral nervous system diseases ; review article |
Keywords: | animal models;axon degeneration;clinical trial;gene therapy;inherited peripheral neuropathy; |
Pubmed / DOI : | Pubmed : 32001243 / DOI : 10.1016/j.brainres.2020.146683 |
N° Profil MNM : | 2020021 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/32001243 |