Title: | Sitting in patients with spinal muscular atrophy type 1 treated with nusinersen |
Journal : | Developmental medicine and child neurology |
Authors: | Aragon Gawinska K, Author ; Daron A ; Ulinici A ; Vanden Brande L ; Seferian A ; Gidaro T ; Scoto M ; Deconinck N ; Servais L |
Material Type: | Article |
Publisher: | England, 12/2019 |
Languages: | English |
Keywords : | antisense oligonucleotides ; cohort studies ; disease evolution ; gene therapy ; motor neuron disease ; neuromuscular disease ; nusinersen ; proximal spinal muscular atrophy type 1 ; sitting position ; SMN1-related proximal spinal muscular atrophy ; spinal muscular atrophy |
Pubmed / DOI : | Pubmed : 31799720 / DOI : 10.1111/dmcn.14412 |
N° Profil MNM : | 2019121 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/31799720 |
See also : |