Titre : | Molecular therapy |
Revue : | Molecular therapy, 26, 9 |
Auteurs : | Collectif, Auteur |
Type de document : | Livre |
Année de publication : | 2018 |
Pages : | p 2077 |
Langues: | Anglais |
Thème : | 19000 (Génétique, protéomique : généralités, techn.) |
Résumé : |
- "iPSC-Derived Cardiomyocytes Taken to Rescue Infarcted Heart Muscle in Coronary Heart Disease Patients", Seppo Ylä-Herttuala
- "Breaking and Sealing Barriers in Retinal Gene Therapy", Joan W. Miller, Luk H. Vandenberghe - "T Cell Tumor Immunotherapy: Oncolysis Beats Lymphodepletion", John Barrett - "Nanotechnology in Wound Care: One Step Closer to the Clinic", Masoud Mozafari - "It’s All in the Delivery: Designing Hydrogels for Cell and Non-viral Gene Therapies", Richard L. Youngblood, Norman F. Truong, Tatiana Segura, Lonnie D. Shea - "Extracellular Vesicles Containing IL-4 Modulate Neuroinflammation in a Mouse Model of Multiple Sclerosis", Giacomo Casella, Federico Colombo, Annamaria Finardi, Hélène Descamps, Gerard Ill-Raga, Antonello Spinelli, Paola Podini, Mattia Bastoni, Gianvito Martino, Luca Muzio, Roberto Furlan - "Exosome-Mediated Small RNA Delivery: A Novel Therapeutic Approach for Inflammatory Lung Responses", Duo Zhang, Heedoo Lee, Xiaoyun Wang, Ashish Rai, Michael Groot, Yang Jin - "Repeated Mesenchymal Stromal Cell Treatment Sustainably Alleviates Machado-Joseph Disease", Catarina Oliveira Miranda, Adriana Marcelo, Teresa Pereira Silva, João Barata, Ana Vasconcelos-Ferreira, Dina Pereira, Clévio Nóbrega, Sónia Duarte, Inês Barros, Joana Alves, José Sereno, Lorena Itatí Petrella, João Castelhano, Vitor Hugo Paiva, Paulo Rodrigues-Santos, Vera Alves, Isabel Nunes-Correia, Rui Jorge Nobre, Célia Gomes, Miguel Castelo-Branco, Luís Pereira de Almeida - "Teriflunomide Modulates Vascular Permeability and Microglial Activation after Experimental Traumatic Brain Injury", Karthik S. Prabhakara, Daniel J. Kota, Gregory H. Jones, Amit K. Srivastava, Charles S. Cox Jr., Scott D. Olson - "AAV5-miHTT Gene Therapy Demonstrates Broad Distribution and Strong Human Mutant Huntingtin Lowering in a Huntington’s Disease Minipig Model", Melvin M. Evers, Jana Miniarikova, Stefan Juhas, Astrid Vallès, Bozena Bohuslavova, Jana Juhasova, Helena Kupcova Skalnikova, Petr Vodicka, Ivona Valekova, Cynthia Brouwers, Bas Blits, Jacek Lubelski, Hana Kovarova, Zdenka Ellederova, Sander J. van Deventer, Harald Petry, Jan Motlik, Pavlina Konstantinova - "Topical Lyophilized Targeted Lipid Nanoparticles in the Restoration of Skin Barrier Function following Burn Wound", Jilong Li, Subhadip Ghatak, Mohamed S. El Masry, Amitava Das, Yang Liu, Sashwati Roy, Robert J. Lee, Chandan K. Sen - "MicroRNA-218-5p Promotes Endovascular Trophoblast Differentiation and Spiral Artery Remodeling", Jelena Brkić, Caroline Dunk, Jacob O’Brien, Guodong Fu, Lubna Nadeem, Yan-ling Wang, David Rosman, Mohamed Salem, Oksana Shynlova, Issaka Yougbaré, Heyu Ni, Stephen J. Lye, Chun Peng - "lncRNA PFAR Promotes Lung Fibroblast Activation and Fibrosis by Targeting miR-138 to Regulate the YAP1-Twist Axis", Xiaoguang Zhao, Jian Sun, Yingzhun Chen, Wei Su, Huitong Shan, Yue Li, Yining Wang, Nan Zheng, Hongli Shan, Haihai Liang - "CD28-zeta CAR T Cells Resist TGF-beta Repression through IL-2 Signaling, Which Can Be Mimicked by an Engineered IL-7 Autocrine Loop", Viktória Golumba-Nagy, Johannes Kuehle, Andreas A. Hombach, Hinrich Abken - "Membrane Stabilization by Modified Steroid Offers a Potential Therapy for Muscular Dystrophy Due to Dysferlin Deficit", Sen Chandra Sreetama, Goutam Chandra, Jack H. Van der Meulen, Mohammad Mahad Ahmad, Peter Suzuki, Shivaprasad Bhuvanendran, Kanneboyina Nagaraju, Eric P. Hoffman, Jyoti K. Jaiswal - "Adenovirus Coding for Interleukin-2 and Tumor Necrosis Factor Alpha Replaces Lymphodepleting Chemotherapy in Adoptive T Cell Therapy", João Manuel Santos, Víctor Cervera-Carrascon, Riikka Havunen, Sadia Zafar, Mikko Siurala, Suvi Sorsa, Marjukka Anttila, Anna Kanerva, Akseli Hemminki - "Combination of Asiatic Acid and Naringenin Modulates NK Cell Anti-cancer Immunity by Rebalancing Smad3/Smad7 Signaling", Guang-Yu Lian, Qing-Ming Wang, Patrick Ming-Kuen Tang, Shuang Zhou, Xiao-Ru Huang, Hui-Yao Lan - "LINC00470 Coordinates the Epigenetic Regulation of ELFN2 to Distract GBM Cell Autophagy", Changhong Liu, Haijuan Fu, Xiaoping Liu, Qianqian Lei, Yan Zhang, Xiaoling She, Qiang Liu, Qing Liu, Yingnan Sun, Guiyuan Li, Minghua Wu - "Retinal AAV8-RS1 Gene Therapy for X-Linked Retinoschisis: Initial Findings from a Phase I/IIa Trial by Intravitreal Delivery", Catherine Cukras, Henry E. Wiley, Brett G. Jeffrey, H. Nida Sen, Amy Turriff, Yong Zeng, Camasamudram Vijayasarathy, Dario Marangoni, Lucia Ziccardi, Sten Kjellstrom, Tae Kwon Park, Suja Hiriyanna, J. Fraser Wright, Peter Colosi, Zhijian Wu, Ronald A. Bush, Lisa L. Wei, Paul A. Sieving - "MicroRNA-125b Interacts with Foxp3 to Induce Autophagy in Thyroid Cancer", Shanshan Wang, Juekun Wu, Jianwei Ren, Alexander C. Vlantis, Ming-yue Li, Shirley Y.W. Liu, Enders K.W. Ng, Amy B.W. Chan, Ding-Cun Luo, Zhimin Liu, Wei Guo, Lingbin Xue, Siu Kwan Ng, C. Andrew van Hasselt, Michael C.F. Tong, George G. Chen - "Correction of Biochemical Abnormalities and Improved Muscle Function in a Phase I/II Clinical Trial of Clenbuterol in Pompe Disease", Dwight D. Koeberl, Laura E. Case, Edward C. Smith, Crista Walters, Sang-oh Han, Yanzhen Li, Wei Chen, Christoph P. Hornik, Kim M. Huffman, William E. Kraus, Beth L. Thurberg, David L. Corcoran, Deeksha Bali, Nenad Bursac, Priya S. Kishnani - "Personalized Cancer Vaccine Platform for Clinically Relevant Oncolytic Enveloped Viruses", Erkko Ylösmäki, Cristina Malorzo, Cristian Capasso, Oona Honkasalo, Manlio Fusciello, Beatriz Martins, Leena Ylösmäki, Antti Louna, Sara Feola, Henrik Paavilainen, Karita Peltonen, Veijo Hukkanen, Tapani Viitala, Vincenzo Cerullo |