Title: | Respiratory assessment in a spinal muscular atrophy infant treated with nusinersen |
Journal : | Pediatrics international : official journal of the Japan Pediatric Society, 61, 10 |
Authors: | Ogawa K, Author ; Okanari K ; Kobayashi O ; Nakashima M ; Ihara K |
Material Type: | Article |
Publisher: | Australia, 10/2019 |
Size: | p 1051 |
Languages: | English |
Keywords : | motor neuron disease ; neuromuscular disease ; nusinersen ; proximal spinal muscular atrophy type 1 ; respiratory features ; SMN1-related proximal spinal muscular atrophy ; spinal muscular atrophy |
Keywords: | nusinersen;spinal muscular atrophy;spontaneous respiration rate;tracheostomy;ventilator |
Pubmed / DOI : | Pubmed : 31612561 / DOI : 10.1111/ped.13931 |
N° Profil MNM : | 2019102 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/31612561 |