Title: | Improved efficacy of a next-generation ERT in murine Pompe disease |
Journal : | JCI insight, 4, 5 |
Authors: | Xu S, Author ; Lun Y ; Frascella M ; Garcia A ; Soska R ; Nair A ; Ponery AS ; Schilling A ; Feng J ; Tuske S ; Valle MCD ; Martina JA ; Ralston E ; Gotschall R ; Valenzano KJ ; Puertollano R ; Do HV ; Raben N ; Khanna R |
Material Type: | Article |
Publication Date: | 07/03/2019 |
Languages: | English |
Pubmed / DOI : | DOI : 10.1172/jci.insight.125358 / Pubmed : 30843882 |
N° Profil MNM : | 2019031 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/30843882 |