Title: | A dystrophic Duchenne mouse model for testing human antisense oligonucleotides |
Journal : | PLoS ONE, 13, 2 |
Authors: | Veltrop M, Author ; van Vliet L ; Hulsker M ; Claassens J ; Brouwers C ; Breukel C ; van der Kaa J ; Linssen MM ; den Dunnen JT ; Verbeek S ; Aartsma Rus A ; van Putten M |
Material Type: | Article |
Publication Date: | 2018 |
Languages: | English |
Keywords : | antisense oligonucleotides ; Duchenne muscular dystrophy ; DYS gene ; dystrophin ; exon skipping ; mouse model ; preclinical trials ; therapeutical research |
Pubmed / DOI : | DOI : 10.1371/journal.pone.0193289 / Pubmed : 29466448 |
N° Profil MNM : | 2018031 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/29466448 |
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