Title: | Myotonic dystrophy: approach to therapy |
Journal : | Current opinion in genetics & development, 44 |
Authors: | Thornton CA, Author ; Wang E ; Carrell EM |
Material Type: | Article |
Publication Date: | 2017 |
Size: | p 135 |
Languages: | English |
Keywords : | DMPK gene ; gène ZNF9 ; interfering RNA ; MBNL protein ; myotonic dystrophy type 1 ; myotonic dystrophy type 2 ; myotonin protein kinase ; preclinical trials ; repeated sequence amplification ; reviews ; toxic RNA ; transcription (genetics) ; ZNF9 protein |
Pubmed / DOI : | DOI : 10.1016/j.gde.2017.03.007 / Pubmed : 28376341 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/28376341 |