Title: | Revised Hammersmith Scale for spinal muscular atrophy: A SMA specific clinical outcome assessment tool |
Journal : | PLoS ONE, 12, 2 |
Authors: | Ramsey D, Author ; Scoto M ; Mayhew A ; Main M ; Mazzone ES ; Montes J ; De Sanctis R ; Dunaway Young S ; Salazar R ; Glanzman AM ; Pasternak A ; Quigley J ; Mirek E ; Duong T ; Gee R ; Civitello M ; Tennekoon G ; Pane M ; Pera MC ; Bushby K ; Day J ; Darras BT ; De Vivo D ; Finkel R ; Mercuri E ; Muntoni F |
Material Type: | Article |
Publication Date: | 2017 |
Languages: | English |
Keywords : | crossover studies ; Hammersmith motor function scale ; SMN1-related proximal spinal muscular atrophy |
Pubmed / DOI : | DOI : 10.1371/journal.pone.0172346 / Pubmed : 28222119 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/28222119 |
See also : |