Title: | ML372 blocks SMN ubiquitination and improves spinal muscular atrophy pathology in mice |
Journal : | JCI insight, 1, 19 |
Authors: | Abera MB, Author ; Xiao J ; Nofziger J ; Titus S ; Southall N ; Zheng W ; Moritz KE ; Ferrer M ; Cherry JJ ; Androphy EJ ; Wang A ; Xu X ; Austin C ; Fischbeck KH ; Marugan JJ ; Burnett BG |
Material Type: | Article |
Publication Date: | 2016 |
Languages: | English |
Pubmed / DOI : | DOI : 10.1172/jci.insight.88427 / Pubmed : 27882347 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/27882347 |