Title: | Patient need versus evidence: a balancing act |
Journal : | Lancet, 388, 10052 |
Authors: | Collectif, Author |
Material Type: | Article |
Publication Date: | 2016 |
Size: | p 1350 |
Languages: | English |
Keywords : | clinical trials ; Duchenne muscular dystrophy ; eteplirsen ; FDA (Food and drug administration) |
Pubmed / DOI : | Pubmed : 27707475 / DOI : 10.1016/S0140-6736(16)31765-2 |