Title: | Full-length Dysferlin Transfer by the Hyperactive Sleeping Beauty Transposase Restores Dysferlin-deficient Muscle |
Journal : | Molecular therapy. Nucleic acids, 5 |
Authors: | Escobar H, Author ; Schowel V ; Spuler S ; Marg A ; Izsvak Z |
Material Type: | Article |
Publication Date: | 2016 |
Languages: | English |
Keywords : | cell therapy ; cellular models ; cross-sectional study ; DYSF gene ; dysferlin ; gene transfer ; immunohistochemistry ; Miyoshi distal myopathy ; mouse model ; scid mouse ; transposable elements |
Pubmed / DOI : | DOI : 10.1038/mtna.2015.52 / Pubmed : 26784637 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/26784637 |