Title: | Oral administration of erythromycin decreases RNA toxicity in myotonic dystrophy |
Journal : | Annals of clinical and translational neurology, 3, 1 |
Authors: | Nakamori M, Author ; Taylor K ; Mochizuki H ; Sobczak K ; Takahashi MP |
Material Type: | Article |
Publication Date: | 2015 |
Size: | p 42 |
Languages: | English |
Keywords : | cellular models ; CTG triplet repeats ; erythromycin ; gène MBNL1 ; myotonic dystrophy type 1 ; neomycin ; oral administration ; splicing ; Steinert mouse ; therapeutic prospects ; toxic RNA |
Pubmed / DOI : | DOI : 10.1002/acn3.271 / Pubmed : 26783549 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/26783549 |
See also : |