Title: | In vivo gene editing in dystrophic mouse muscle and muscle stem cells |
Journal : | Science (New York, N.Y.), 351, 6271 |
Authors: | Tabebordbar M, Author ; Zhu K ; Cheng JKW ; Chew WL ; Widrick JJ ; Yan WX ; Maesner C ; Wu EY ; Xiao R ; Ran FA ; Cong L ; Zhang F ; Vandenberghe LH ; Church GM ; Wagers AJ |
Material Type: | Article |
Publication Date: | 2016 |
Size: | p 407 |
Languages: | English |
Keywords : | adenoassociated vectors ; CRISPR/Cas9 ; Duchenne muscular dystrophy ; exon skipping ; gene expression ; mdx mouse |
Abstract: |
Comment in:
Genetic engineering: In vivo genome editing - growing in strength. [Nat Rev Genet. 2016] CRISPR/Cas9 Flexes Its Muscles: In Vivo Somatic Gene Editing for Muscular Dystrophy. [Mol Ther. 2016] |
Pubmed / DOI : | DOI : 10.1126/science.aad5177 / Pubmed : 26721686 |