Title: | Biotherapies of neuromuscular disorders : Biothérapies des maladies neuromusculaires |
Journal : | Revue neurologique, 170, 12 |
Authors: | Briand JF ; Roy MO ; Mourlane F ; André C ; Loux N ; Rougeau C ; Toursel T ; Braun S |
Material Type: | Article |
Publication Date: | 2014 |
Size: | p 799 |
Languages: | English |
Keywords : | cell therapy ; CRISPR/Cas9 ; cross-sectional study ; exon skipping ; gene therapy ; monoclonal antibodies ; motor neurons ; myasthenia gravis ; restriction enzyme ; review article ; skeletal muscle |
Keywords: | Anticorps monoclonaux;Biotherapies;Biothérapies;Gene therapy;Modulation de l’ARN;Monoclonal antibodies;Motoneuron;Motoneurone;Muscle;RNA modulation;Thérapie génique; |
Pubmed / DOI : | DOI : 10.1016/j.neurol.2014.07.018 / Pubmed : 25459122 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/25459122 |