Title: | Observational study of spinal muscular atrophy type I and implications for clinical trials |
Journal : | Neurology, 83, 9 |
Authors: | Finkel RS ; McDermott MP ; Kaufmann P ; Darras BT ; Chung WK ; Sproule DM ; Kang PB ; Foley AR ; Yang ML ; Martens WB ; Oskoui M ; Glanzman AM ; Flickinger J ; Montes J ; Dunaway S ; O'Hagen J ; Quigley J ; Riley S ; Benton M ; Ryan PA ; Montgomery M ; Marra J ; Gooch C ; de Vivo DC |
Material Type: | Article |
Publication Date: | 2014 |
Size: | p 810 |
Languages: | English |
Keywords : | clinical presentation ; clinical trials ; cross-sectional study ; disease natural history ; guidelines ; loongitudinal study ; observational research ; proximal spinal muscular atrophy type 1 |
Pubmed / DOI : | DOI : 10.1212/WNL.0000000000000741 / Pubmed : 25080519 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/25080519 |