Title: | AAV1.NT-3 gene therapy for Charcot-Marie-Tooth neuropathy |
Journal : | Molecular therapy, 22, 3 |
Authors: | Sahenk Z ; Galloway G ; Clark KR ; Malik V ; Rodino-Klapac LR ; Kaspar B ; Chen L ; Braganza C ; Montgomery C ; Mendell JR |
Material Type: | Article |
Publication Date: | 2014 |
Size: | p. 511-521 |
Languages: | English |
Keywords : | adenoassociated vectors ; CMT1A ; cross-sectional study ; demyelination ; electrodiagnosis ; gene therapy ; histopathology ; motor skills ; myelination ; neurotrophin 3 ; peripheral nerves ; Schwann cells ; trembler mouse |
Pubmed / DOI : | DOI : 10.1038/mt.2013.25 / Pubmed : 24162799 |
See also : |