Title: | Enzyme replacement therapy in the mouse model of Pompe disease |
Journal : | Molecular genetics and metabolism, 80 |
Authors: | Raben N ; Danon MJ ; Gilbert AL ; Dwivedi S ; Bosnoyan-Collins LO ; Thurberg BL ; Mattaliano RJ ; Nagaraju K ; Plotz PH |
Material Type: | Article |
Publication Date: | 2003 |
Size: | p. 159-169 |
Languages: | English |
Keywords : | acid alpha-glucosidase ; animal models ; enzymotherapy ; glycogen ; mouse model ; Pompe disease ; skeletal muscle ; therapeutic prospects |