Title: | Thérapies enzymatiques substitutives des maladies lysosomales |
Journal : | médecine/sciences (m/s), 21, n° spécial |
Authors: | Germain DP |
Material Type: | Article |
Publication Date: | 11/2005 |
Size: | p. 77-83 |
Languages: | French |
Keywords : | clinical trials ; enzymes ; Fabry disease ; Gaucher disease ; lysosomal diseases ; medical treatment ; mucopolysaccharidosis ; Niemann-Pick disease ; orphan drugs ; photographies ; Pompe disease |
Abstract: |
Accès au résumé PubMed / to PubMed abstract |
Lien associé : | http://www.ncbi.nlm.nih.gov/entrez/query.fcgi?cmd=Retrieve&db=pubmed&dopt=Abstract&list_uids=16324679&query_hl=18&itool=pubmed_docsum |