Title: | Exploring the frontiers of therapeutic exon skipping for Duchenne muscular dystrophy by double targeting within one or multiple exons |
Journal : | Molecular therapy, 14, 3 |
Authors: | Aartsma Rus A ; Kaman WE ; Weij R ; den Dunnen JT ; van Ommen GJB ; van Deutekom JCT |
Material Type: | Article |
Publication Date: | 2006 |
Size: | p. 401-407 |
Languages: | English |
Keywords : | antisense oligonucleotides ; Becker muscular dystrophy ; Duchenne muscular dystrophy ; dystrophin ; exon ; exon skipping ; gene therapy ; molecular genetics ; splicing |
Abstract: |
Accès au résumé PubMed / to PubMed abstract |
Lien associé : | http://www.ncbi.nlm.nih.gov/entrez/query.fcgi?db=pubmed&cmd=Retrieve&dopt=AbstractPlus&list_uids=16753346&query_hl=7&itool=pubmed_docsum |