Title: | New developments in the treatment of Pompe disease (Steps forward in Pompe disease 3rd European Symposium) |
Journal : | Clinical Therapeutics |
Authors: | Steps forward in Pompe disease 3rd European Symposium (20-21/11/2009; Munich (Allemagne)) ; Mattaliano RJ |
Material Type: | Article |
Publication Date: | 2010 |
Size: | 32, Suppl. B, p. S55-S56 |
Languages: | English |
Keywords : | acid alpha-glucosidase ; adulthood ; clinical trials ; enzyme activity ; enzymotherapy ; gene therapy ; glycogen ; medical treatment ; mouse model ; Pompe disease ; skeletal muscle ; symposium ; viral vectors |
Pubmed / DOI : | DOI : 10.1016/S0149-2918(10)00081-0 |