Title: | Clinical experience, implications, and expectations of treatment with alglucosidase alfa in infants (Steps forward in Pompe disease 3rd European Symposium) |
Journal : | Clinical Therapeutics |
Authors: | Steps forward in Pompe disease 3rd European Symposium (20-21/11/2009; Munich (Allemagne)) ; Nicolino M |
Material Type: | Article |
Publication Date: | 2010 |
Size: | 32, Suppl. B, p. S57 |
Languages: | English |
Keywords : | acid alpha-glucosidase ; assisted ventilation ; children ; clinical trials ; death ; early-onset Pompe disease ; enzymotherapy ; glycogen ; hypertrophic cardiomyopathy ; invasive ventilation ; muscle weakness ; Pompe disease ; respiratory failure ; skeletal muscle ; symposium ; Taiwan |
Pubmed / DOI : | DOI : 10.1016/S0149-2918(10)00080-9 |