Title: | Antisense-oligonucleotide mediated exon skipping in activin-receptor-like kinase 2 : inhibiting the receptor that is overactive in fibrodysplasia ossificans progressiva |
Journal : | PLoS ONE, 8, 7, e69096 |
Authors: | Shi S ; Cai J ; de Gorter DJJ ; Sanchez-Duffhues G ; Kemaladewi DU ; Hoogaars WMH ; Aartsma Rus A ; t Hoen PAC ; Ten Dijke P |
Material Type: | Article |
Publication Date: | 2013 |
Size: | 7 p. |
Languages: | English |
Keywords : | ACVR1 gene ; ACVR1 receptors ; antisense oligonucleotides ; exon skipping ; fibrodysplasia ossificans progressiva ; genetic mutations ; heterotopic ossifications ; mouse model |
Abstract: |
Accès au résumé PubMed / to PubMed abstract |
Lien associé : | http://www.ncbi.nlm.nih.gov/pubmed/23861958 |
Pubmed / DOI : | DOI : 10.1371/journal.pone.0069096 |