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Author Church K |
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Mendell JR ; Pozsgai ER ; Lewis S ; Griffin DA ; Lowes LP ; Alfano LN ; Lehman KJ ; Church K ; Reash NF ; Iammarino MA ; Sabo B ; Potter R ; Neuhaus S ; Li X ; Stevenson H ; Rodino-Klapac LR | 01/2024Article
Mendell JR ; Sahenk Z ; Lehman KJ ; Lowes LP ; Reash NF ; Iammarino MA ; Alfano LN ; Lewis S ; Church K ; Shell R ; Potter RA ; Griffin DA ; Hogan M ; Wang S ; Mason S ; Darton E ; Rodino-Klapac LR | 14/08/2023Article
Jackson JL ; Korth CX ; Leslie CE ; Cotto J ; Mah ML ; Hor K ; Cripe L ; Al Zaidy S ; Camino EM ; Church K ; Lehman KJ ; Shay V ; Mendell JR | United States | 09/10/2020Article
Mendell JR ; Sahenk Z ; Lehman K ; Nease C ; Lowes LP ; Miller NF ; Iammarino MA ; Alfano LN ; Nicholl A ; Al Zaidy S ; Lewis S ; Church K ; Shell R ; Cripe LH ; Potter RA ; Griffin DA ; Pozsgai E ; Dugar A ; Hogan M ; Rodino-Klapac LR | 06/2020Article
Lowes LP, Author ; Alfano LN ; Arnold WD ; Shell R ; Prior TW ; McColly M ; Lehman KJ ; Church K ; Sproule DM ; Nagendran S ; Menier M ; Feltner DE ; Wells C ; Kissel JT ; Al Zaidy S ; Mendell J | United States | 05/2019Article
Mendell JR, Author ; Chicoine LG ; Al Zaidy SA ; Sahenk Z ; Lehman K ; Lowes L ; Miller N ; Alfano L ; Galliers B ; Lewis S ; Murrey D ; Peterson E ; Griffin DA ; Church K ; Cheatham S ; Cheatham J ; Hogan MJ ; Rodino-Klapac LR | 19/04/2019Article
Al Zaidy S, Author ; Pickard AS ; Kotha K ; Alfano LN ; Lowes L ; Paul G ; Church K ; Lehman K ; Sproule DM ; Dabbous O ; Maru B ; Berry K ; Arnold WD ; Kissel JT ; Mendell JR ; Shell R | 02/2019Article
Mendell JR, Author ; Sahenk Z ; Al Zaidy S ; Rodino-Klapac LR ; Lowes LP ; Alfano LN ; Berry K ; Miller N ; Yalvac M ; Dvorchik I ; Moore-Clingenpeel M ; Flanigan KM ; Church K ; Shontz K ; Curry C ; Lewis S ; McColly M ; Hogan MJ ; Kaspar BK | 2017Comment in: Unfounded Claims of Improved Functional Outcomes Attributed to Follistatin Gene Therapy in Inclusion Body Myositis. [Mol Ther. 2017] Reply to Letter to the Editor. [Mol Ther. 2017]Article
Mendell JR, Author ; Al Zaidy S ; Shell R ; Arnold WD ; Rodino-Klapac LR ; Prior TW ; Lowes L ; Alfano L ; Berry K ; Church K ; Kissel JT ; Nagendran S ; L'Italien J ; Sproule DM ; Wells C ; Cardenas JA ; Heitzer MD ; Kaspar A ; Corcoran S ; Braun L ; Likhite S ; Miranda C ; Meyer K ; Foust KD ; Burghes AHM ; Kaspar BK | 2017Comment in The Dilemma of Two Innovative Therapies for Spinal Muscular Atrophy. [N Engl J Med. 2017] Motor neuron disease: Positive trial results published for ground-breaking SMA therapies. [Nat Rev Neurol. 2018] Therapy for Spin[...]