Title: | Unmet Therapeutic Needs of Non-Ambulatory Patients with Duchenne Muscular Dystrophy: A Mixed-Method Analysis |
Journal : | Therapeutic innovation & regulatory science |
Authors: | Schuster ALR ; Crossnohere NL ; Fischer R ; Furlong P ; Bridges JFP |
Material Type: | Article |
Publication Date: | 24/03/2022 |
Languages: | English |
Keywords : | adulthood ; caregivers ; Duchenne muscular dystrophy ; inquiries ; quality of life ; therapeutic efficiency |
Keywords: | Patient reported outcome measures;Patient-focused drug development;Rare diseases; |
Lien associé : | Texte complet disponible sur PubMed Central (PMC) |
Pubmed / DOI : | Pubmed : 35325439 / DOI : 10.1007/s43441-022-00389-x |
N° Profil MNM : | 2022032 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/35325439 |