Title: | National registry of patients with Fukuyama congenital muscular dystrophy in Japan |
Journal : | Neuromuscular disorders : NMD, 28, 10 |
Authors: | Ishigaki K ; Ihara C ; Nakamura H ; Mori Yoshimura M ; Maruo K ; Taniguchi-Ikeda M ; Kimura E ; Murakami T ; Sato T ; Toda T ; Kaiya H ; Osawa M |
Material Type: | Article |
Publication Date: | 10/2018 |
Size: | p. 885 |
Languages: | French |
Keywords: | FKTN;Fukuyama congenital muscular dystrophy;Japan Muscular Dystrophy Association (JMDA);Natural history;Patient registry; |
Pubmed / DOI : | Pubmed : 30220444 / Pubmed : 10.1016/j.nmd.2018.08.001 |