Title: | Safety, tolerability and clinical efficacy of nusinersen in SMA type 1 older than 7 months: a prospective study |
Journal : | Neuromuscular disorders : NMD, 27, s2 |
Authors: | Aragon Gawinska K ; Gargaun E ; Seferian A ; Gidaro T ; Gilabert S ; Lilien C ; Vuillerot C ; Cances C ; Daron A ; Marucco E ; De A ; Flet Berliac L ; Armier H ; Fiedler L ; Servais L |
Material Type: | Article |
Publication Date: | 2017 |
Size: | s211 |
Languages: | English |
Abstract: |
Poster présenté lors :
22nd International Congress of the World Muscle Society 3-7 October 2017 • St Malo, France Volume 27, Supplement 2, Pages S51-S270 (October 2017) |
Pubmed / DOI : | DOI : 10.1016/j.nmd.2017.06.422 |