Title: | The SMA Clinical Trial Readiness Program: creation and evaluation of a program to enhance SMA trial readiness in the United States |
Journal : | Orphanet journal of rare diseases, 15, 1 |
Authors: | Peterson I ; Cruz R ; Sarr F ; Stanley AM ; Jarecki J |
Material Type: | Article |
Publisher: | England, 05/2020 |
Size: | p 118 |
Languages: | English |
Keywords : | clinical trials ; public health ; review article ; spinal muscular atrophy |
Keywords: | clinical trial best practices;clinical trial coordination;clinical trial readiness;physical therapist and evaluator readiness;rare disease;rare disease clinical trial;spinal muscular atrophy; |
Pubmed / DOI : | Pubmed : 32443972 / DOI : 10.1186/s13023-020-01387-8 |
N° Profil MNM : | 2020052 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/32443972 |
See also : |