Title: | Structure-Specific Cleavage of an RNA Repeat Expansion with a Dimeric Small Molecule Is Advantageous over Sequence-Specific Recognition by an Oligonucleotide |
Journal : | ACS chemical biology |
Authors: | Benhamou RI ; Angelbello AJ ; Andrews RJ ; Wang ET ; Moss WN ; Disney MD |
Material Type: | Article |
Publisher: | United States, 01/2020 |
Languages: | English |
Keywords : | antisense oligonucleotides ; cell cultures ; in vitro ; myotonic dystrophy ; myotonic dystrophy type 2 ; neuromuscular disease ; therapeutical research |
Pubmed / DOI : | Pubmed : 31927948 / DOI : 10.1021/acschembio.9b00958 |
N° Profil MNM : | 2020012 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/31927948 |