Title: | Oligonucleotides to the (Gene) Rescue: FDA Approvals 2017-2019 |
Journal : | Trends in pharmacological sciences, 41, 1 |
Authors: | Ruger J ; Ioannou S ; Castanotto D ; Stein CA |
Material Type: | Article |
Publisher: | England, 01/2020 |
Size: | p 27 |
Languages: | English |
Keywords : | antisense oligonucleotides ; drug marketing regulation in France ; economy ; gene therapy ; nusinersen ; patisiran ; review article |
Keywords: | Onpattro;SMA;SMN;spinraza;tegsedi;hATTR; |
Pubmed / DOI : | Pubmed : 31836192 / DOI : 10.1016/j.tips.2019.10.009 |
N° Profil MNM : | 2019122 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/31836192 |