Title: | Targeted PMP22 TATA-box editing by CRISPR/Cas9 reduces demyelinating neuropathy of Charcot-Marie-Tooth disease type 1A in mice |
Journal : | Nucleic acids research |
Authors: | Lee JS, Author ; Lee JY ; Song DW ; Bae HS ; Doo HM ; Yu HS ; Lee KJ ; Kim HK ; Hwang H ; Kwak G ; Kim D ; Kim S ; Hong YB ; Lee JM ; Choi BO |
Material Type: | Article |
Publisher: | England, 11/2019 |
Languages: | English |
Keywords : | Charcot-Marie-Tooth disease ; CMT1A ; CRISPR ; CRISPR/Cas9 ; gene therapy ; mouse ; peripheral nervous system diseases ; PMP22 gene ; promoters (genetics) ; RESEARCH |
Pubmed / DOI : | Pubmed : 31713617 / DOI : 10.1093/nar/gkz1070 |
N° Profil MNM : | 2019112 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/31713617 |
See also : |