Title: | Improvement of spinal muscular atrophy via correction of the SMN2 splicing defect by Brucea javanica (L.) Merr. extract and Bruceine D |
Journal : | Phytomedicine : international journal of phytotherapy and phytopharmacology, 65 |
Authors: | Baek J, Author ; Jeong H ; Ham Y ; Jo YH ; Choi M ; Kang M ; Son B ; Choi S ; Ryu HW ; Kim J ; Shen H ; Sydara K ; Lee SW ; Kim SY ; Han SB ; Oh SR ; Cho S |
Material Type: | Article |
Publisher: | Germany, 09/2019 |
Languages: | English |
Keywords : | complementary medicine ; motor neuron disease ; neuromuscular disease ; RESEARCH ; SMN1-related proximal spinal muscular atrophy ; SMN2 gene |
Keywords: | Alternative splicing;Brucea javanica, Bruceine D;Neuromuscular disease;Spinal muscular atrophy (SMA);Splicing modulator; |
Pubmed / DOI : | Pubmed : 31563042 / DOI : 10.1016/j.phymed.2019.153089 |
N° Profil MNM : | 2019093 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/31563042 |
See also : |