Title: | Ataluren use in patients with nonsense mutation Duchenne muscular dystrophy: patient demographics and characteristics from the STRIDE Registry |
Journal : | Journal of comparative effectiveness research |
Authors: | Muntoni F, Author ; Desguerre I ; Guglieri M ; Osorio AN ; Kirschner J ; Tulinius M ; Buccella F ; Elfring G ; Werner C ; Schilling T ; Trifillis P ; Zhang O ; Delage A ; Santos CL ; Mercuri E |
Material Type: | Article |
Publisher: | England, 08/2019 |
Languages: | English |
Pubmed / DOI : | Pubmed : 31414621 / DOI : 10.2217/cer-2019-0086 |
N° Profil MNM : | 2019082 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/31414621 |
See also : |