Title: | Selective modulation of the androgen receptor AF2 domain rescues degeneration in spinal bulbar muscular atrophy |
Journal : | Nature medicine |
Authors: | Badders NM, Author ; Korff A ; Miranda HC ; Vuppala PK ; Smith RB ; Winborn BJ ; Quemin ER ; Sopher BL ; Dearman J ; Messing J ; Kim NC ; Moore J ; Freibaum BD ; Kanagaraj AP ; Fan B ; Tillman H ; Chen PC ; Wang Y ; Iii BBF ; Li Y ; Kim HJ ; La Spada AR ; Taylor JP |
Material Type: | Article |
Publication Date: | 05/03/2018 |
Languages: | English |
Keywords : | androgen receptor ; androgen receptor related disease ; Kennedy disease ; mouse model ; physiopathology ; preclinical trials ; spinal and bulbar muscular atrophy ; therapeutic prospects |
Pubmed / DOI : | DOI : 10.1038/nm.4500 / Pubmed : 29505030 |
N° Profil MNM : | 2018031 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/29505030 |
See also : |