Title: | Eteplirsen for paediatric patients with Duchenne muscular dystrophy: A pooled-analysis |
Journal : | Journal of clinical neuroscience : official journal of the Neurosurgical Society of Australasia, 49 |
Authors: | Randeree L, Author ; Eslick GD |
Material Type: | Article |
Publication Date: | 2018 |
Languages: | English |
Keywords : | 6 minute walk test ; children ; controversy ; drug marketing regulation in France ; Duchenne muscular dystrophy ; dystrophin ; eteplirsen ; exon skipping ; FDA (Food and drug administration) ; muscle fibers ; reviews ; skeletal muscle ; therapeutic efficiency |
Keywords: | AVI-4658;DMD;Dystrophin fibres;Eteplirsen;Walk test; |
Pubmed / DOI : | DOI : 10.1016/j.jocn.2017.10.082 / Pubmed : 29254734 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/29254734 |
See also : |