Title: | Making Sense of Antisense Oligonucleotides: A Narrative Review |
Journal : | Muscle & Nerve, 57, 3 |
Authors: | Goyal N, Author ; Narayanaswami P |
Material Type: | Article |
Publication Date: | 2018 |
Size: | p 356 |
Languages: | English |
Keywords : | amyotrophic lateral sclerosis ; antisense oligonucleotides ; biochemistry ; bioethics ; clinical trials ; Duchenne muscular dystrophy ; eteplirsen ; exon skipping ; familial amyloid neuropathy ; gene expression ; gene therapy ; messenger RNA ; modes of action ; molecular structure ; morpholinos ; myotonic dystrophy type 1 ; nusinersen ; prix du médicament ; review article ; reviews ; routes of administration ; SMN1-related proximal spinal muscular atrophy ; splicing ; therapeutic efficiency |
Keywords: | Duchenne muscular dystrophy;antisense oligonucleotides;eteplirsen;nusinersen;spinal muscular atrophy; |
Pubmed / DOI : | DOI : 10.1002/mus.26001 / Pubmed : 29105153 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/29105153 |