Title: | Morpholino-mediated Knockdown of DUX4 Toward Facioscapulohumeral Muscular Dystrophy Therapeutics |
Journal : | Molecular therapy : the journal of the American Society of Gene Therapy, 24, 8 |
Authors: | Chen JC, Author ; King OD ; Zhang Y ; Clayton NP ; Spencer C ; Wentworth BM ; Emerson CP Jr ; Wagner KR |
Material Type: | Article |
Publication Date: | 2016 |
Size: | p 1405 |
Languages: | English |
Keywords : | cellular models ; DUX4 gene ; electroporation ; facioscapulohumeral muscular dystrophy ; gene expression ; interfering RNA ; morpholinos ; mouse model ; myotube ; silencers (genetics) ; therapeutic prospects ; xenografts |
Pubmed / DOI : | DOI : 10.1038/mt.2016.111 / Pubmed : 27378237 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/27378237 |