Title: | Duchenne muscular dystrophy drugs face tough path to approval |
Journal : | Drugs of today (Barcelona, Spain : 1998), 52, 3 |
Authors: | Hodgkinson L, Author ; Sorbera L ; Graul AI |
Material Type: | Article |
Publication Date: | 2016 |
Size: | p 199 |
Languages: | English |
Keywords : | drisapersen ; Duchenne muscular dystrophy ; eteplirsen ; exon skipping ; FDA (Food and drug administration) ; guidelines ; orphan drugs ; phase 3 clinical trials |
Keywords: | Drisapersen;Duchenne muscular dystrophy;eteplirsen; |
Pubmed / DOI : | Pubmed : 27186594 / DOI : 10.1358/dot.2016.52.3.2473590 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/27186594 |