Title: | CRISPR/Cas9 treatment for Duchenne muscular dystrophy |
Journal : | Cell Research, 26, 5 |
Authors: | Mendell JR, Author ; Rodino-Klapac LR |
Material Type: | Article |
Publication Date: | 2016 |
Size: | p 513 |
Languages: | English |
Keywords : | adenoassociated vectors ; CRISPR/Cas9 ; Duchenne muscular dystrophy ; exon skipping ; mdx mouse ; therapeutic prospects |
Abstract: |
Comment on:
Evidence-based path to newborn screening for Duchenne muscular dystrophy. [Ann Neurol. 2012] |
Pubmed / DOI : | DOI : 26926391 / DOI : 10.1038/cr.2016.28 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/26926391 |