Title: | A large animal model of Spinal Muscular Atrophy and correction of phenotype |
Journal : | Annals of neurology, 77, 3 |
Authors: | Duque SI, Author ; Arnold WD ; Odermatt P ; Li X ; Porensky PN ; Schmelzer L ; Meyer K ; Kolb SJ ; Schumperli D ; Kaspar BK ; Burghes AH |
Material Type: | Article |
Publication Date: | 2015 |
Size: | p 399 |
Languages: | English |
Keywords : | AAV9 vectors ; animal models ; biological markers ; gene therapy ; motor neurons ; pig ; SMN1 gene |
Pubmed / DOI : | DOI : 10.1002/ana.24332 / Pubmed : 25516063 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/25516063 |
See also : |