Title: | Molecular therapeutic strategies for spinal muscular atrophies : current and future clinical trials |
Journal : | Clinical Therapeutics, 36, 1 |
Authors: | Zanetta C ; Nizzardo M ; Simone C ; Monguzzi E ; Bresolin N ; Comi GP ; Corti S |
Material Type: | Article |
Publication Date: | 2014 |
Size: | p. 128-140 |
Languages: | English |
Keywords : | antisense oligonucleotides ; clinical trials ; cross-sectional study ; gene therapy ; medical treatment ; molecular genetics ; review article ; reviews ; SMN protein ; spinal muscular atrophy |
Pubmed / DOI : | DOI : 10.1016/j.clinthera.2013.11.006 / Pubmed : 24360800 |