Title: | Overview on DMD exon skipping |
Journal : | Methods in molecular biology, 867, Chap 7 |
Authors: | Aartsma Rus A |
Material Type: | Article |
Publication Date: | 2012 |
Size: | p. 97-116 |
Languages: | English |
Keywords : | antisense oligonucleotides ; clinical trials ; drisapersen ; Duchenne muscular dystrophy ; dystrophin ; exon skipping ; model dog ; mouse model ; review article |