Title: | Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning |
Journal : | Science, 296 |
Authors: | Aiuti A ; Slavin S ; Aker M ; Ficara F ; Deola S ; Mortellaro A ; Morecki S ; Andolfi G ; Tabucchi A ; Carlucci F ; Marinello E ; Cattaneo F ; Vai S ; Servida P ; Miniero R ; Roncarolo MG ; Bordignon C |
Material Type: | Article |
Publication Date: | 28/06/2002 |
Size: | p. 2410-2413 |
Languages: | English |
Keywords : | B cells ; cell therapy ; clinical trials ; enzyme activity ; gene therapy ; genetic vectors ; myoadenylate deaminase deficiency ; PCR ; stem cells ; T cells ; X-linked severe combined immunodeficiency |
Abstract: |
Accès au résumé PubMed / to PubMed abstract |
Lien associé : | http://www.ncbi.nlm.nih.gov/entrez/query.fcgi?db=pubmed&cmd=Retrieve&dopt=AbstractPlus&list_uids=12089448&query_hl=21&itool=pubmed_docsum |